Clinical trials are research studies that are designed to determine if a medicine is safe and effective for patients.
People who choose to participate in clinical trials play a critical role in developing new medicines, particularly for rare diseases and conditions that are especially difficult to treat. Whenever possible, Agios will refer an individual requesting access to our investigational medicines to an appropriate clinical trial.
For more information about Agios’ ongoing clinical trials, visit our Clinical Trials or visit clinicaltrials.gov and search "Agios." To discuss your eligibility for an Agios clinical trial, please ask your doctor to contact us on your behalf at 844-633-2332 or firstname.lastname@example.org.
In some cases, patients with serious or immediately life-threatening diseases may not be eligible for any clinical trials and may not have other treatment options. Generally, and only in rare and very specific circumstances, these patients may be able to receive investigational medicines outside the clinical trial process through "Expanded Access Programs" (sometimes referred to as "Compassionate Use").
EAPs are for people with serious or life-threatening diseases who have exhausted all treatment options and are not eligible for any appropriate clinical trials. Generally, there are two types of EAPs: 1) those for individuals, and 2) those for groups. In all cases, local health authority approval of the EAP is required.